Eligibility

• PI must hold an academic appointment at the Assistant Professor level or higher
• Preclinical studies must be complete
• If an FDA Investigational New Drug (IND) application is necessary for the proposed clinical study, the IND application should already have passed FDA initial review and be active 
• If the PI has recruited additional patient enrollment sites, local IRB approval must be obtained for each site.

Program Specific Evaluation Criteria

• How many treatment options would this study provide for children?
• How accessible is this study for children and families to access?